FDA grants Orphan Drug Designation to LFB’s « Complement Factor H »
français du Fractionnement et des Biotechnologies) with the Orphan Designation for its
Complement Factor H, a human plasma-derived product, currently in pre-clinical
development.
The designated orphan indication is for the "Treatment of atypical Hemolytic Uremic
Syndrome (aHUS) associated with an inherited abnormality of the complement system".
For more information, please visit www.lfb.fr
Isn't it a great news? :)))
Comment
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Comment by Linda Burke on March 1, 2010 at 3:12pm -
No way! Don't be at all sorry, Zofia .... by putting this exciting info in your front page Blog you're helping to raise awareness of something very valuable 'in the pipeline'. I can't wait for someone to hear about the next steps for this wonderful development. I can understand LBF's need to keep things hush-hush because of the proprietary nature, but I'm just so curious to learn the details! Thanks in advance for keeping an eye out for any more news on this front- we'd appreciate it an update whenever possible. With appreciation, Linda
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Comment by Cheryl Biermann on March 1, 2010 at 9:59am -
Way to go Zofia, it's amazing you found this information, excellent! Let us know any further developments. Thanks.
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Comment by Zofia on March 1, 2010 at 4:19am -
Sorry Linda :). Next time I’ll check our page better before writing something. But I’ll definitely try to find some more info about that treatment.
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Comment by Linda Burke on February 28, 2010 at 1:58pm
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Thanks Zofia, for raising awareness in your blog and bringing this to everyone's attention. In the 'Current Research' Forum, Joy Lewis has a 27kb pdf version filed in her Feb 14th post. Thanks to Mireya in Spain who alerted Joy to the information for posting in the Current Research Forum.
Zofia, this IS a most interesting trail to follow - as yet we have uncovered no further leads but we can't wait to find out any further info you discover on the human-derived Factor H product. Thanks so much for your blog!
WELCOME - Friends, Family Members, Patients, and Researchers - JOIN US!
The Foundation for Children with Atypical HUS encourages patients and investigators to share information and explore options/resources as we work together to gain insight into this rare complement disorder. By increasing contact opportunities with researchers and medical personnel interested in helping the aHUS community, our stories foster a better understanding of atypical hemolytic uremic syndrome.
Sharing information, inspiration and support for one another, we seek to gather together people and knowledge as we strive to improve the lives of patients and families dealing with a diagnosis of aHUS.
NEW DIAGNOSIS OF aHUS?
Be proactive! Get the medical basics of aHUS, what lab values to monitor, and areas of concern...check out the "aHUS Bootcamp" and "About aHUS" tabs at the top of this page!
If your doctor has never treated a case of aHUS, please print out our 'Doc to Doc Registry' and ask him/her to contact a physician versed in the complexities of aHUS and new options for 2011 genetic testing and treatment.
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Did you know...
• • • • • • • • • • • •
It is estimated that there are about 300 cases of aHUS in the U.S., and it is most common with young children. The condition is life threatening and either can be chronic or can recur at intervals.
more factoids...
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